D2I2.
genetic

Lesch–Nyhan syndrome

Lesch–Nyhan (LNS) is a rare inherited disorder caused by a of the hypoxanthine-guanine phosphoribosyltransferase (HGPRT). This deficiency occurs due to in the HPRT1 gene located on the X . LNS affects about 1 in 380,000 live births. The disorder was first recognized and clinically characterized by American medical student Michael Lesch and his mentor, pediatrician William Nyhan, at Johns Hopkins.

Underlined words are explained — tap any of them.

Symptoms — what it feels like

  • ·self harm, dystonia, chorea, spasticity, intellectual disability, hyperuricemia

Complications

  • ·kidney failure, megaloblastic

Outlook

  • ·cite web
  • ·url=https://rarediseases.org/rare-diseases/lesch-nyhan-/
Plain-language summary adapted from Wikipedia. Not medical advice.